Rare Diseases

U.S. FDA Approves First Treatment for Cerebrotendinous Xanthomatosis
February 23, 2025

Tampere University, Theravia Partner to Advance New EB Drug
February 19, 2025



Epidermolysis Bullosa: A Clinical Review and Update
May 21, 2024

CBD Cream Shows Promise in EB
May 21, 2024

Congenital Ichthyosis Update
May 14, 2024

