Rare Diseases

Done Deal: LEO Pharma Closes Deal for BI’s Spesolimab (Spevigo)
October 2, 2025






U.S. FDA Approves First Treatment for Cerebrotendinous Xanthomatosis
February 23, 2025

Tampere University, Theravia Partner to Advance New EB Drug
February 19, 2025



Epidermolysis Bullosa: A Clinical Review and Update
May 21, 2024

CBD Cream Shows Promise in EB
May 21, 2024

